A New Hope in the Treatment of Rett Syndrome: Trofinetide

Authors : Doğancan Sönmez

Pages : 134-135

Doi:10.38175/phnx.1465288

View : 65 | Download : 62

Publication Date : 2024-11-01

Article Type : Other Papers

Abstract :Trofinetide is a medication used to treat Rett Syndrome. It was approved by the United States in March 2023 for the treatment of Rett Syndrome in adults and children ages 2 and older. The drug is an N-terminal tripeptide derivative of insulin-like growth factor-1 (IGF-1) and is an oral, small molecule, synthetic analogue. The FDA\'s approval of trophinetide marks the first authorized treatment for Rett Syndrome.
Keywords : Rett Sendromu, Tedavi, Trofinetid